Exonics Therapeutics is developing gene editing therapies to treat patients with Duchenne Muscular Dystrophy (DMD) and other severe genetic neuromuscular diseases, utilizing SingleCut CRISPR technology to repair and restore dystrophin
Exonics Therapeutics is developing gene editing therapies to treat patients with Duchenne Muscular Dystrophy (DMD) and other severe genetic neuromuscular diseases, utilizing SingleCut CRISPR technology to repair and restore dystrophin.