Biotechnology company developing therapeutics for complex age-related diseases using a proprietary in vivo drug discovery platform
Biotechnology company developing therapeutics for complex age-related diseases using a proprietary in vivo drug discovery platform. Its Patient Avatars, Mosaic Screening, and Pythia platform test pooled libraries of hundreds of interventions in diseased animals and analyze transcriptomic effects across cellular pathways. The company reports programs across six disease areas, including an osteoarthritis candidate in IND-enabling studies, and is advancing an AAV gene therapy toward the clinic.